How useful would you find lectures on the following topics (all related to gene therapy for NMDs) for your daily practice?

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* 1. Educational: The basics of gene therapy

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* 2. Preclinical: Viral vector technology

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* 3. Preclinical: How to build and optimize a gene therapy viral vector

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* 4. Preclinical: Non viral gene therapy

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* 5. Clinical experience: Overview of currently ongoing gene therapy clinical trials

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* 6. Clinical experience: Patient perspective

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* 7. Clinical experience: What is involved in running a gene therapy trial at your center?

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* 8. Clinical experience: Ongoing clinical trials for MTM and DMD

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* 9. Clinical experience: Trial design

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* 10. Clinical experience: Inflammatory response and pre-existing antibodies

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* 11. Clinical experience: Trial readiness

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* 12. Clinical experience: Communication with patients (expectations and risks)

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* 13. Approved gene therapy products: Current state of the art for Zolgensma

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* 14. Approved gene therapy products: Patient perspective

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* 15. Approved gene therapy products: Prescribing gene therapy products

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* 16. Approved gene therapy products: How to monitor for side effects?

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* 17. Approved gene therapy products: Early access programmes

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* 18. Approved gene therapy products: Pricing and access

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* 19. Concerns: Ethical aspects

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* 20. Concerns: Patient perception (hype)

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* 21. Concerns: What do we know about acute and long term safety and side effects?

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* 22. Concerns: Lessons learned from gene therapy NMD trials

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* 23. Concerns: Gene therapy and inflammatory response

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* 24. Future perspective: Future of gene therapy

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